Because the accumulative number of people with rare disease is substantial, it is pointed out that treating and helping these people benefits the whole community.
February 28, 2018 marks the 11th annual Rare Disease Day, dedicated to raising awareness of the impact of rare diseases worldwide.
年までに50余りが市場に届き、治療選択肢の限られた希少疾患に新たな希望をもたらすだろう。
By 2030, it is expected that more than 50 agents will reach the market and bring new hope to patients with rare conditions that have limited efficacious treatment options.
The diagnosis of a rare disease such as Duchenne muscular dystrophy is often a life-changing event, but there are many organisations dedicated to helping patients and their families.
Rare Disease patient findings Eularis utilize the power of sophisticated Artificial Intelligence powered software and the internet to leave breadcrumbs to lead potential patients, and the doctors treating them, to the drug for their condition.
Learn more about the organizations allied with the rare disease community and raising awareness of rare diseases like HPP, LAL-D, aHUS, and PNH, as well as how you can help the cause.
Let our multi-disciplinary experts put their experience to work to advance your rare disease drug development program and transform obstacles into opportunities.
Rare Disease Day was established in Europe in 2008 by EURORDIS, the organization representing rare disease patients in Europe, and is now observed in more than 80 nations.
For instance, some companies have started to adopt more diversified models, expanding their focus to encompass more rare diseases, generics, biosimilars, OTC and vaccines.
Dear pemphigus& pemphigoid Community, As you know, the IPPF and the rare disease community have been working with Congress to advance the 21st Century Cures Act(HR 6).
Target Diseases As a distinguishing characteristics of Nagoya University Hospital, many patients with malignant neoplasms, intractable or rare diseases are target of rehabilitation therapy.
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